Oncology Focused Pipeline​

The core value of OBI lies in its passion to develop and deliver a portfolio of unique antibody-drug conjugates (ADCs) drugs for patients, in addition to its promising Globo H active immunotherapy. This evolving portfolio includes a spectrum of cancer targets, such as TROP2, Nectin-4, HER2, and other potential targets.​​

This table provides an overview of our pipeline. ​

Molecule Name

Target

Potential Indications

Status

Modality

Molecule Name

OBI-992

Target:

TROP2

Potential Indications:

Solid Tumors

Status:

Phase 1

Modality:

ADC

OBI-992 is a TROP2-targeted antibody-drug conjugate (ADC) that carries a potent topoisomerase I inhibitor, exatecan, via a hydrophilic, enzyme-cleavable linker. OBI-992 remains stable in circulation but delivers the cytotoxic payload to TROP2-expressing tumor cells, leading to tumor cell death while avoiding off-target toxicities. TROP2 is highly expressed in a variety of solid tumors with no or low expression in normal tissues, rendering it an ideal target for cancer therapy.​

OBI-992 demonstrates unique target-binding characteristics, superior antitumor efficacy, improved pharmacokinetics, and a favorable safety profile in preclinical in vitro and in vivo models. The results of animal studies were published and featured as the cover story in the February 2025 issue of “Molecular Cancer Therapeutics”. The in vitro findings were published in “Scientific Reports” in March 2025. The outstanding preclinical results support further clinical development of OBI-992. ​

U.S. FDA cleared an IND application for a Phase 1/2 Study of OBI-992 in Jan 2024 (ClinicalTrials.gov: NCT06480240) and has been approved by US FDA for Orphan Drug Designation for the treatment of gastric cancer in Aug 2024. The Phase 1/2 study is currently enrolling patients in the United States and Taiwan (OBI-992-001) to evaluate OBI-992’s safety, PK, and preliminary efficacy. No dose-limiting toxicities were observed to date.

The TROP2 targeting antibody was in-licensed from Biosion, Inc. in Dec 2021.

Molecule Name

OBI-902

Target:

TROP2

Potential Indications:

Solid Tumors

Status:

Preclinical

Modality:

ADC

OBI-902 is the next generation TROP2-targeted ADC. OBI-902 is the first ADC powered by OBI’s proprietary glycan-based platform GlycOBI®, a dual-function enzyme, EndoSymeOBI®, and a novel linker technology, HYPrOBI™.

Preclinical data of OBI-902 indicate that GlycOBI® is an efficient platform to generate homogeneous ADCs with an efficient and scalable process under GMP conditions. Compared to benchmark TROP2 ADCs, OBI-902 demonstrated favorable PK and differentiated profiles with excellent stability in circulation, extended exposure in tumors, and durable antitumor activity in various cancer models. A favorable safety profile of OBI-902 was shown in a repeat dose toxicity study in monkeys. These results will be presented in two separate posters at AACR 2025 in Chicago.

U.S. FDA cleared an IND application for a Phase 1/2 Study of OBI-902 in April 2025.

Molecule Name

OBI-904

Target:

Nectin-4

Potential Indications:

Solid Tumors

Status:

Preclinical

Modality:

ADC

OBI-904 is an antibody-drug conjugate (ADC) comprising a monoclonal antibody specifically targeting Nectin-4 (Nectin cell adhesion molecule 4), linked to a potent topoisomerase I inhibitor payload through OBI’s proprietary GlycOBI® ADC enabling technologies, powered by a dual-function enzyme, EndoSymeOBI®, and a novel linker technology, HYPrOBI™. It is a novel and potentially first-in-class and best-in-class glycan-based ADC designed to target multiple cancer types that express Nectin-4.

Molecule Name

OBI-201

Target:

TROP2 x HER2

Potential Indications:

Undisclosed

Status:

Preclinical

Modality:

BsADC

OBI-201 is a TROP2 x HER2 bispecific ADC generated by OBI GlycOBI® ADC enabling technologies, powered by a dual-function enzyme, EndoSymeOBI®, and a novel linker technology, HYPrOBI™, and conjugated with topoisomerase I inhibitor, exatecan. OBI-201 offers several advantages over mono-specific TROP2 or HER2 ADCs. By targeting both antigens, it broadens tumor coverage, especially in cancers with heterogeneous or low expression of either marker. Dual targeting can enhance tumor selectivity, binding strength, and internalization, improving payload delivery to cancer cells while potentially reducing off-tumor toxicity. It may also overcome resistance mechanisms associated with single-antigen therapies by retaining efficacy if . Given tumors’ heterogeneous nature, it ensures more efficient drug distribution, and targeting both HER2 and TROP2 may produce synergistic anti-tumor effects through multiple pathways. These combined benefits could lead to improved efficacy and durability of response compared to mono-therapeutic ADCs.

Molecule Name

BsADC / Dual Payload ADC

Target:

Undisclosed

Potential Indications:

Undisclosed

Status:

Discovery

Modality:

BsADC

Bispecific ADCs have emerged as promising modalities for cancer therapeutics. OBI continues to develop bispecific ADCs with new targets and dual payload design to increase pipeline diversity. By targeting dual antigens, BsADC can potentially overcome resistance mechanisms that arise from the downregulation or mutation of a single target antigen. The broader targeting approach not only enhances specificity but is also expected to improve efficacy while reducing toxicity, thereby expanding the patient population that could benefit from these treatments. OBI’s next generation bispecific ADC, can either utilize the proprietary GlycOBI® technologies, powered by a dual-function enzyme, EndoSymeOBI®, and a novel linker technology, HYPrOBI™, or GlycOBI DUO™ technology, which allows two distinct cytotoxic payloads exerting a more flexible and more effective BsADC. OBI’s next generation BsADC represents an advanced development in this field.

Molecule Name

OBI-833

Target:

Globo H

Potential Indications:

Lung (NSCLC)

Status:

Phase 2

Modality:

Active Immunotherapy

OBI-833 is a novel active immunotherapy for cancer, targeting the tumor surface glycan antigen Globo H. Globo H is linked to the carrier protein diphtheria toxin CRM197. Upon administration into the body, it stimulates the production of antibodies against Globo H by the immune cells, aiming to treat cancer.

Molecule Name

OBI-3424

Target:

AKR1C3

Potential Indications:

Liver (HCC) and T-ALL

Status:

Phase 2

Modality:

Prodrug

OBI-3424 is a first-in-class novel chemotherapeutic prodrug that can selectively act on a variety of cancers with overexpression of Aldo-keto reductase family 1 member C3 (AKR1C3). OBI-3424 has been granted Orphan Drug Designation (ODD) for the treatment of hepatocellular carcinoma (HCC) and acute lymphocytic leukemia (ALL). Clinical trials of HCC and ALL (NCT04315324) are in collaboration with Ascentawits* (CTR20201915) and SWOG Cancer Research Network (NCT04315324), respectively.

*OBI acquired the worldwide rights (except for China, Hong Kong, Macao, Taiwan, Japan, South Korea, Singapore, Malaysia, Thailand, Turkey, and India; owned by Ascentawits as AST-3424) of OBI-3424 from Threshold Pharmaceuticals, Inc. in.

Expanded Access

STATEMENT OF OBI’S POSITION ON EXPANDED ACCESS (COMPASSIONATE USE)

OBI Pharma, Inc. (together with its wholly-owned subsidiary OBI Pharma USA, Inc., “OBI Pharma”) is a clinical stage biotechnology company committed to the development of safe and effective products for use in oncology areas of high unmet medical need. Our goal is to make available access to our unapproved products (investigational products) through participation in clinical trials and through expanded access programs. Expanded access programs allow for the use of investigational products outside a clinical trial when the primary purpose is to treat a serious, life-threatening condition.

In cases where a clinical trial is not an option, and the patient has exhausted all available treatment options, regulators/health authorities may grant permission for us to provide a treating physician with an investigational product pre-approval. Such individual use of an investigational product pre-approval is often called “expanded access” or “compassionate use” though other names may be used. OBI Pharma commonly refers to these requests as “expanded access”.

OBI Pharma is committed to making available our unapproved products (investigational products) through expanded access in cases where:

  • the patient’s condition is severe or life-threatening,
  • the patient has exhausted all other approved treatment options that the patient is able to tolerate, and
  • the patient is ineligible to participate in existing clinical trials.

Access to an investigational product is possible when:

  • the investigational product is actively being used in clinical trials and not approved for the indication in the jurisdiction concerned,
  • there is sufficient clinical data available for the investigational product and the disease condition to anticipate that any potential benefit from treatment is likely to outweigh any potential risks to the patient,
  • there is adequate data to permit selection of an appropriate dose level for the patient,
  • there is sufficient product supply to support both the ongoing clinical trials and the expanded access request, and
  • the expanded access request will not compromise the integrity of ongoing clinical trials or delay regulatory filings.

OBI Pharma may discontinue expanded‑access supply for an individual patient or program if (i) clinical data reveal an unfavorable risk–benefit profile, (ii) supply becomes unavailable, or (iii) regulatory authorities request suspension.

Our partnership with treating physicians:

The treating physician is solely responsible for overseeing patient treatment and safety. The physician is also solely responsible for obtaining Health Authority and Institutional Review Board approvals and patient consent prior to use.

Learn More:

If you are a physician who is interested in learning more about our investigational products, or participating in our clinical trials, please submit a request to expandedaccess@obipharma.com. We anticipate acknowledging receipt of requests sent to this email within five business days.

If you are a patient who is interested in accessing our investigational products, please speak with your physician. If you have additional questions, please contact expandedaccess@obipharma.com. You may also learn more about ongoing clinical trials by going to www.clinicaltrials.gov.

 

DISCLAIMER: An existing program does not guarantee availability in all jurisdictions. Various regulatory mechanisms exist in different jurisdictions to provide Early Access to new medicines and as a result, jurisdiction-specific variations for Early Access will occur. Any Early Access to medicines must always comply with the applicable jurisdiction-specific laws and regulations including investigational product importation requirements.